Access to generic Risdiplam sought under policy for rare diseases for people with Spinal Muscular Atrophy

Persons living with Spinal Muscular Atrophy (SMA), and parents of minor persons living with the condition, have written to Prime Minister Narendra Modi seeking his urgent intervention to ensure nationwide access to generic Risdiplam under the National Policy for Rare Diseases (NPRD).

SMA is a genetic, progressive, and life-limiting neuromuscular condition, and access to treatment is time sensitive, with delays having the potential to cause irreversible deterioration.